Duchenne Muscular Dystrophy | IPS Therapeutique

Duchenne Muscular Dystrophy

Duchenne Muscular Dystrophy (DMD), a genetic disorder causing muscle degeneration, that affects 1 in 3,500 male births. It leads to loss of ambulation, respiratory failure, and heart complications, impacting life expectancy and quality of life. Early intervention and therapies are critical for improving outcomes.

Duchenne Muscular Dystrophy - Readouts & Application

Readouts:

Application:

This model is crucial for evaluating the effectiveness of novel drug compounds aimed at correcting the underlying genetic mutations in DMD, as well as addressing the muscle degeneration, fibrosis, and impaired regeneration characteristic of the disease.